CLINICAL TRIAL OF GENE THERAPY FOR ADA-DEFICIENT SCID
- 3 Anni 2003/2006
 - 2.784.422€ Totale Fondi
 
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Pubblicazioni Scientifiche
- 2004-03-01 HUMAN GENE THERAPY 
Mobilized blood CD341 cells transduced and selected with a clinically applicable protocol reconstitute lymphopoiesis in SCID-Hu mice
 - 2004-12-01 MOLECULAR THERAPY 
IL-3 or IL-7 increases ex vivo gene transfer efficiency in ADA-SCID BM CD34+ cells while maintaining in vivo lymphoid potential